+ Create post

uniQure reports longer Huntington’s follow-up, with mixed statistical results

uniQure ($QURE) released additional Phase I/II results for AMT-130 in Huntington’s disease. Among 15 high-dose patients followed for 36 months, the company reported 80% slower decline on the composite disease-rating scale against an external natural-history control. At 48 months, 12 high-dose patients showed 44% slowing on that scale, but the comparison was not statistically significant, with p=0.144. Functional-capacity results remained nominally significant. The longer follow-up informs the du

0
0